Modified Lentiviral Globin Gene Therapy for Pediatric β0/β0 Transfusion-Dependent β-Thalassemia: A Single-Center, Single-Arm Pilot Trial

Published: 17 April 2024| Version 2 | DOI: 10.17632/8rrszmkw89.2
Contributor:
Fangyuan Hao

Description

These data are the deposited supplemental information for the article entitled "Modified Lentiviral Globin Gene Therapy for Pediatric β0/β0 Transfusion-Dependent β-Thalassemia: A Single-Center, Single-Arm Pilot Trial" by Shiqi Li and Sikai Ling et al. in Cell Stem Cell

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Gene Therapy, Lentivirus, Beta Thalassemia

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