Clinically relevant AAV8-PEX1 gene therapy preserves retinal integrity and function long-term in a murine model of Zellweger spectrum disorder

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This dataset contains the source numerical data used in the manuscript “Clinically relevant AAV8‑PEX1 gene therapy preserves retinal integrity and function long‑term in a murine model of Zellweger spectrum disorder.” Included files: ERG source traces (dose‑finding, high‑dose, long‑term), OMR numerical data, and LC‑MS/MS lipidomics datasets (raw vendor files and processed peak tables).

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