Cerebrospinal Fluid 24(S)-hydroxycholesterol levels post intrathecal adrabetadex infusion

Description

Cerebrospinal fluid 24(S)-hydroxycholesterol levels pre administration and 48 hours after intrathecal administration of adrabetadex (2-hydroxypropyl-B-cyclodextrin. Data relative to sex, age, age of neurological onset, NPC neurological severity score without hearing, and Annual Severity Increment Score.

Steps to reproduce

Would have to obtain samples from an ongoing clinical trial or request material.

Institutions

• National Institute of Child Health and Human Development

  MD, Bethesda

Categories

Funders

• Eunice Kennedy Shriver National Institute of Child Health and Human Development

  Maryland, United States

  Grant ID: ZIA HD008989
• Eunice Kennedy Shriver National Institute of Child Health and Human Development

  Maryland, United States

  Grant ID: ZIA HD008988

Licence