Therapeutic base editing of HBG promoter to reactivate high level of γ-globin expression with no detectable off-target mutations

Name: Therapeutic base editing of HBG promoter to reactivate high level of γ-globin expression with no detectable off-target mutations
Creator: ying zhang
Published: 2023-09-11T17:06:17.176Z
Keywords: Hematopoietic Stem Cell Transplantation, Beta Thalassemia

zhang, ying; Qiu, Houyuan

doi:10.17632/sf7zywbswy.2

Therapeutic base editing of HBG promoter to reactivate high level of γ-globin expression with no detectable off-target mutations

Published: 11 September 2023| Version 2 | DOI: 10.17632/sf7zywbswy.2

Contributors:

ying zhang, Houyuan Qiu

Description

raw FACS data of fetal hemoglobin expression in HSPCs and bone marrow transplantation experiments in NBSGW mice

Therapeutic base editing of HBG promoter to reactivate high level of γ-globin expression with no detectable off-target mutations

Description

Files

Categories

Licence